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AN OPEN-LABEL, ASCENDING-DOSE, FIRST-INHUMAN STUDY TO ASSESS THE SAFETY, TOLERABILITY, AND PHARMACOKINETICS OF INTRAVENOUS INFUSIONS OF ATB200 ALONE AND ATB200 CO-ADMINISTERED WITH ORAL AT2221 IN ADULT SUBJECTS WITH POMPE DISEASE

Clinical Trial Grant
Duke Scholars

Administered By

Pediatrics, Medical Genetics

Awarded By

Amicus Therapeutics Corporation

Start Date

April 1, 2016

End Date

September 30, 2017
 

Administered By

Pediatrics, Medical Genetics

Awarded By

Amicus Therapeutics Corporation

Start Date

April 1, 2016

End Date

September 30, 2017