A retrospective chart review study to assess the clinical outcome of triheptanoin treatment in patients with long-chain fatty acid oxidation disorders (LC-FAOD) treated under expanded access program
Clinical Trial Grant
Administered By
Pediatrics, Medical Genetics
Awarded By
Ultragenyx Pharmaceutical
Start Date
January 22, 2019
End Date
September 30, 2020
Administered By
Pediatrics, Medical Genetics
Awarded By
Ultragenyx Pharmaceutical
Start Date
January 22, 2019
End Date
September 30, 2020