PHASE 3 STUDY EVALUATING GENE THERAPY BY TRANSPLANTATION OF AUTOLOGOUS CD34+ STEM CELLS TRANSDUCED EX VIVO WITH THE LENTIGLOBIN BB305 LENTIVIRAL VECTOR IN SUBJECTS WITH SEVERE SICKLE CELL DISEASE
Administered By
Awarded By
Contributors
- Martin, Paul Langlie Principal Investigator
Start/End
- April 17, 2020 - March 29, 2022