Liver-directed AAV gene therapy for PHKG2-Glycogen Storage Disease IX (GSD IX y2)
Administered By
Awarded By
Contributors
- Bali, Deeksha Sarihyan Mentor
- Clinton, Lani Kai Mentor
- Kishnani, Priya Sunil Principal Investigator
- Young, Sarah Phyllis Mentor
Start/End
- September 1, 2021 - August 31, 2024