Evaluation of children with the "late-onset" Pompe disease GAA variants identified by newborn screening: Guidance for in person or virtual monitoring
Clinical Trial Grant
Administered By
Pediatrics, Medical Genetics
Awarded By
Genzyme Corporation
Start Date
May 19, 2021
End Date
April 30, 2025
Administered By
Pediatrics, Medical Genetics
Awarded By
Genzyme Corporation
Start Date
May 19, 2021
End Date
April 30, 2025