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Evaluation of children with the "late-onset" Pompe disease GAA variants identified by newborn screening: Guidance for in person or virtual monitoring

Clinical Trial Grant
Duke Scholars

Administered By

Pediatrics, Medical Genetics

Awarded By

Genzyme Corporation

Start Date

May 19, 2021

End Date

April 30, 2025
 

Administered By

Pediatrics, Medical Genetics

Awarded By

Genzyme Corporation

Start Date

May 19, 2021

End Date

April 30, 2025