A Phase 3, Randomized, Double-blind, Placebo-controlled Study of Adeno-associated Virus Serotype 8-mediated Gene Transfer of Glucose-6-phosphatase in Patients With Glycogen Storage Disease Type Ia
Clinical Trial Grant
Administered By
Pediatrics, Medical Genetics
Awarded By
Ultragenyx Pharmaceutical
Start Date
September 3, 2021
End Date
September 30, 2024
Administered By
Pediatrics, Medical Genetics
Awarded By
Ultragenyx Pharmaceutical
Start Date
September 3, 2021
End Date
September 30, 2024