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An Open-Label Study to Evaluate the Efficacy, Safety and Pharmacokinetics, Pharmacodynamics, and Immunogenicity of Cipaglucosidase Alfa/Miglustat in both ERT Experienced and ERT Naive Pediatric Subjects with Infantile- Onset Pompe Disease Aged 0 < 18

Clinical Trial Grant
Duke Scholars

Administered By

Pediatrics, Medical Genetics

Awarded By

Amicus Therapeutics, Inc.

Start Date

March 9, 2023

End Date

October 31, 2026
 

Administered By

Pediatrics, Medical Genetics

Awarded By

Amicus Therapeutics, Inc.

Start Date

March 9, 2023

End Date

October 31, 2026