An Open-Label Study to Evaluate the Efficacy, Safety and Pharmacokinetics, Pharmacodynamics, and Immunogenicity of Cipaglucosidase Alfa/Miglustat in both ERT Experienced and ERT Naive Pediatric Subjects with Infantile- Onset Pompe Disease Aged 0 < 18
Clinical Trial Grant
Administered By
Pediatrics, Medical Genetics
Awarded By
Amicus Therapeutics, Inc.
Start Date
March 9, 2023
End Date
October 31, 2026
Administered By
Pediatrics, Medical Genetics
Awarded By
Amicus Therapeutics, Inc.
Start Date
March 9, 2023
End Date
October 31, 2026