An Open-label, Multinational, Multicenter, Intravenous Infusion Study of the Efficacy, Saftey, Pharmacokinetics, and Pharmacodynamics of Avalglucosidase Alfa in Treatment-naive Pediatric Participants with Infantile-Onset Pompe Disease (IOPD)
Clinical Trial Grant
Administered By
Pediatrics, Medical Genetics
Awarded By
Sanofi US
Start Date
October 20, 2022
End Date
August 1, 2028
Administered By
Pediatrics, Medical Genetics
Awarded By
Sanofi US
Start Date
October 20, 2022
End Date
August 1, 2028