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An Open-label, Multinational, Multicenter, Intravenous Infusion Study of the Efficacy, Saftey, Pharmacokinetics, and Pharmacodynamics of Avalglucosidase Alfa in Treatment-naive Pediatric Participants with Infantile-Onset Pompe Disease (IOPD)

Clinical Trial Grant
Duke Scholars

Administered By

Pediatrics, Medical Genetics

Awarded By

Sanofi US

Start Date

October 20, 2022

End Date

August 1, 2028
 

Administered By

Pediatrics, Medical Genetics

Awarded By

Sanofi US

Start Date

October 20, 2022

End Date

August 1, 2028