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A Prospective observational study to describe outcomes of alglucosidase alfa treatment in patients <6 months of age with infantile-onset Pompe disease (IOPD)

Clinical Trial Grant
Duke Scholars

Administered By

Pediatrics, Medical Genetics

Awarded By

Sanofi US

Start Date

December 7, 2022

End Date

April 1, 2024
 

Administered By

Pediatrics, Medical Genetics

Awarded By

Sanofi US

Start Date

December 7, 2022

End Date

April 1, 2024