A Prospective observational study to describe outcomes of alglucosidase alfa treatment in patients <6 months of age with infantile-onset Pompe disease (IOPD)
Clinical Trial Grant
Administered By
Pediatrics, Medical Genetics
Awarded By
Sanofi US
Start Date
December 7, 2022
End Date
April 1, 2024
Administered By
Pediatrics, Medical Genetics
Awarded By
Sanofi US
Start Date
December 7, 2022
End Date
April 1, 2024