Gene Ther
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Publication Venue For
- Viral vector gene delivery of the novel chaperone protein SRCP1 to modify insoluble protein in in vitro and in vivo models of ALS. 2021
- Human carbonic anhydrase-8 AAV8 gene therapy inhibits nerve growth factor signaling producing prolonged analgesia and anti-hyperalgesia in mice.. 25:297-311. 2018
- Prevalence of AAV1 neutralizing antibodies and consequences for a clinical trial of gene transfer for advanced heart failure.. 23:313-319. 2016
- Rescue administration of a helper-dependent adenovirus vector with long-term efficacy in dogs with glycogen storage disease type Ia.. 19:443-452. 2012
- Neutralizing antibodies against adeno-associated virus examined prospectively in pediatric patients with hemophilia.. 19:288-294. 2012
- Peptide affinity reagents for AAV capsid recognition and purification.. 18:1020-1024. 2011
- Hydrostatic isolated limb perfusion with adeno-associated virus vectors enhances correction of skeletal muscle in Pompe disease.. 17:1500-1505. 2010
- A small regulatory element from chromosome 19 enhances liver-specific gene expression.. 16:43-51. 2009
- Bioluminescent virion shells: new tools for quantitation of AAV vector dynamics in cells and live animals.. 15:1618-1622. 2008