Molecular Therapy : the Journal of the American Society of Gene Therapy
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Publication Venue For
- In Situ Gene Therapy via AAV-CRISPR-Cas9-Mediated Targeted Gene Regulation.. 26:1818-1827. 2018
- In Vivo Expansion and Antitumor Activity of Coinfused CD28- and 4-1BB-Engineered CAR-T Cells in Patients with B Cell Leukemia.. 26:976-985. 2018
- Polymer-Mediated Inhibition of Pro-invasive Nucleic Acid DAMPs and Microvesicles Limits Pancreatic Cancer Metastasis.. 26:1020-1031. 2018
- Immunization with an SIV-based IDLV Expressing HIV-1 Env 1086 Clade C Elicits Durable Humoral and Cellular Responses in Rhesus Macaques.. 24:2021-2032. 2016
- The AAV vector toolkit: poised at the clinical crossroads.. 20:699-708. 2012
- Phase 1 gene therapy for Duchenne muscular dystrophy using a translational optimized AAV vector.. 20:443-455. 2012
- Engineering and selection of shuffled AAV genomes: a new strategy for producing targeted biological nanoparticles.. 16:1252-1260. 2008
- RNA aptamer-targeted inhibition of NF-kappa B suppresses non-small cell lung cancer resistance to doxorubicin.. 16:66-73. 2008
- In vivo treatment of hemophilia A and mucopolysaccharidosis type VII using non-primate lentiviral vectors. 3:850-856. 2001