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Pediatrics

Organization

Featured Grants


Skeletal muscle-targeted gene therapy for Pompe disease

Research · Awarded by National Institutes of Health · 2025 - 2030

Alveolar injury and repair in Pompe Disease

Research · Awarded by National Institutes of Health · 2025 - 2028

Optimizing Gene Therapy for Respiratory Insufficiency in Duchenne Muscular Dystrophy

Research · Awarded by National Heart, Lung, and Blood Institute · 2024 - 2028