Pediatrics, Neurology

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  People

  • Administrative Positions

    • Mikati, Mohamad Abdul, Chief, Division of Pediatric Neurology

  • Professorships

    • Mikati, Mohamad Abdul, Wilburt C. Davison Distinguished Professor

  • Primary Appointments

    • Gospe Jr., Sidney M., Adjunct Professor in the Department of Pediatrics
    • Jasien, Joan Mary, Assistant Professor of Pediatrics
    • Kansagra, Sujay Mansukhlal, Associate Professor of Pediatrics
    • Lachiewicz, Ave Maria, Associate Professor of Pediatrics
    • Lemmon, Monica Elizabeth, Assistant Professor of Pediatrics
    • Lewis Jr., Darrell Vincent, Professor of Pediatrics
    • Mikati, Mohamad Abdul, Professor of Pediatrics
    • Pizoli, Carolyn Elizabeth, Assistant Professor of Pediatrics
    • Rathke, Kevin Marc, Clinical Associate in the Department of Pediatrics
    • Smith, Edward Clinton, Associate Professor of Pediatrics
    • Tchapyjnikov, Dmitry, Assistant Professor of Pediatrics
    • Valdez, Purnima Thyagarajan, Assistant Professor of Pediatrics
    • Werner, Klaus-Georg Erich, Assistant Professor of Pediatrics
    • Worley, Gordon, Professor Emeritus of Pediatrics
    • Zafar, Muhammad Shahzad, Assistant Professor of Pediatrics

  • Secondary Appointments

    • Ashley, David, Professor in Pediatrics
• 

  Administers Grant

  • 2019 PPMD CDCC Grant
  • A Comprehensive Newborn Screening Solution for Duchenne and Congenital Muscular Dystrophies
  • A Double-Blind, Placebo-Controlled, Randomized-Withdrawal, Multicenter Study of the Efficacy and Safety of Xyrem with an Open-Label Pharmacokinetic Evaluation and Safety Extension in Pediatric Subjects with Narcolepsy with Cataplexy
  • A Double-blind, Randomized, Placebo-controlled Trial of Adjunctive Ganaxolone Treatment in Children and Young Adults with Cyclin-dependent Kinase-like 5 (CDKL5) Deficiency Disorder (CDD) Followed by Long-term Open-label Treatment
  • A Learning Healthcare System for Pediatric Epilepsy
  • A Long-term Follow-up Study of Patients in the Clinical Trials for Spinal Muscular Atrophy Receiving AVXS-101
  • A Long-term Observational Study Evaluating Eteplirsen in Patients with Duchenne Muscular Dystrophy under Conditions of Routine Clinical Practice
  • A MULTICENTER, DOUBLE-BLIND, RANDOMIZED, PLACEBO-CONTROLLED, PARALLEL-GROUP STUDY TO INVESTIGATE THE EFFICACY AND SAFETY OF LACOSAMIDE AS ADJUNCTIVE THERAPY IN SUBJECTS WITH EPILEPSY >1 MONTH TO <4 YEARS OF AGE WITH PARTIAL-ONSET SEIZURES
  • A MULTICENTER, OPEN-LABEL STUDY TO EVALUATE THE PHARMACOKINETICS, SAFETY, AND TOLERABILITY OF INTRAVENOUS BRIVARACETAM IN SUBJECTS ¿1 MONTH TO <16 YEARS OF AGE WITH EPILEPSY PHASE 2
  • A MULTICENTER, OPEN-LABEL, LONG-TERM EXTENSION STUDY TO INVESTIGATE THE EFFICACY AND SAFETY OF LACOSAMIDE AS ADJUNCTIVE THERAPY IN PEDIATRIC SUBJECTS WITH EPILEPSY WITH PARTIAL-ONSET SEIZURES PHASE 3
  • A Phase 2 Study to Assess the Safety, Tolerability, Exploratory Efficacy, and Pharmacokinetics of Orally Administered JBPOS0101 for Refractory Infantile Spasms Patients
  • A Retrospective Multicenter Study to Investigate Dosage, Efficacy,and Safety of Fycompa® in Routine Clinical Care of Patients With Epilepsy
  • A Two-Part Study of ZX008 in Children and Adults with Lennox-Gastaut Syndrome (LGS)
  • A double-blind, randomized, placebo-controlled trial of adjunctive ganaxolone treatment in female children with protocadherin 19 (PCDH19)-related epilepsy followed by long-term open-label treatment
  • ATPA2 Research Project
  • An Observational Study to Investigate Cognition and Quality of Life in Children and Adolescents with Dravet Syndrome (Pro00102865)
  • An Open-label Extension Study for Patients with Spinal Muscular Atrophy who Previously Participated in Investigation Studies of ISIS 396443
  • Bloodwork_Clinical Outcomes Duchenne MD Therapeutic Trials-UCD0305
  • CINRG CHAR0312 Duchenne Muscular Dystrophy Tissue Bank for Exon Skipping
  • CINRG PITT0112 Becker Muscular Dystrophy-A Natural History Study to Predict Efficacy of Exon Skipping
  • CLN3: Modulation of Apoptosis and Ceramide Levels
  • Catastrophic outcomes in the AHC knock-in mouse models D801 N and E815K for ACH
  • Clinical Meaningful Outcomes for Duchenne Muscular Dystrophy Therapeutic Trials
  • Clinical Meaningful Outcomes for Duchenne Muscular Dystrophy Therapeutic Trials
  • Consequences of prolonged febrile seizures in childhood
  • Consequences of prolonged febrile seizures in childhood
  • Continued anticonvulsants after resolution of neonatal seizures: a patient-centered comparative effectiveness study
  • Control Of Ionic Channels By Intracellular Calcium
  • Decision Making for Critically Ill Infants
  • Decision Making for Infants with Neurologic Conditions
  • E2007-G000-238 Perampanel for <2 yrs
  • Endogenous Opiods: Their Role In Ltp In Dentate Gyrus
  • Endogenous Opioids Regulate LTP of Inhibition
  • Endogenous Opioids Regulate Ltp Of Inhibition
  • Endogenous Opioids: Their Role In Ltp In Dentate Gyrus
  • Gaba-B Mediated Disinhibition In The Dentate Gyrus
  • Gabab Mediated Disinhibition In The Dentate Gyrus
  • Gabab Mediated Disinhibition In The Dentate Gyrus
  • Ion Channel Control By Calcium
  • LivaNova Core Registry
  • Microburst VNS Therapy Feasibility Study in Subjects with Refractory Epilepsy
  • Neonatal Seizure Registry Developmental Functional EValuation (NSR-DEV)
  • Network Plasticity in Pediatric Traumatic Brain Injury- A Structural and Functional MRI Study of Network Plasticity in Pediatric Traumatic Brain Injury
  • NeuroSpeak: Developing a curriculum in delivering bad news for medical students in neurology
  • Neurotransmitter Modulation Of Intracellular Calcium
  • No question too small: Development of a question prompt list for infants and their families
  • OPEN-LABEL, SINGLE-ARM, MULTICENTER, LONG-TERM STUDY TO EVALUATE SAFETY AND EFFICACY OF BRIVARACETAM USED AS ADJUNCTIVE TREATMENT IN PEDIATRIC SUBJECTS WITH EPILEPSY
  • PEACE (Pegzilarginase Effect on Arginase 1 Deficiency Clinical Endpoints): A Randomized, Double-Blind, Placebo-Controlled Phase 3 Study of the Efficacy and Safety of Pegzilarginase in Children and Adults with Arginase 1 Deficiency
  • PPMD Research Liaison Grant
  • PPMD Research Liaison Grant
  • Pathophysiology of the AHC Knock-in Mouse Model
  • Pediatric Status Epilepticus Research Group
  • Ph I Zecuity
  • Phase I, Open-Label Study of Carisbamate in Adult and Pediatric Subjects with Lennox-Gastaut Syndrome
  • Phase I, Open-Label, Pharmacokinetic, Dose Escalation Study of Carisbamate in Adult and Pediatric Subjects with Lennox-Gastaut Syndrome
  • Preventing Epilepsy Using Vigabatrin in Infants With Tuberous Sclerosis Complex (PREVeNT Trial)
  • SMA Care Center Registry
  • Spasm Prediction After SyMptomatic neonatal seizures - the SPASM study
  • VBP-15-002 A Phase IIa Open-Label, Multiple Ascending Dose study to assess the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Exploratory Efficacy of Vamorolone in Boys with Duchenne Muscular Dystrophy (DMD)
  • VBP15-003 A Phase II Open-label, Multicenter Extension Study to Assess the Long-term Safety and Efficacy of Vamorolone in Boys with Duchenne Muscular Dystrophy (DMD)

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