The emerging natural history of cross-reactive immunologic material (CRIM)-negative infantile Pompe disease patients treated with recombinant human GAA


Conference Paper

Full Text

Duke Authors

Cited Authors

  • Sheets, KB; Kishnani, PS; Kazi, Z; DeArmey, SM; Bali, DS; Dai, J; Rehder, CW

Published Date

  • February 2014

Published In

Volume / Issue

  • 111 / 2

Start / End Page

  • S97 - S97

Published By

International Standard Serial Number (ISSN)

  • 1096-7192

Digital Object Identifier (DOI)

  • 10.1016/j.ymgme.2013.12.237