Pilot study of adjunctive albuterol in late-onset Pompe disease reveals safety and efficacy from upregulated Mannose-6-phosphate receptor expression

Published

Conference Paper

Full Text

Published version (via Digital Object Identifier)

Duke Authors

Cited Authors

Koeberl, D; Austin, S; Case, L; Smith, EC; Buckley, A; Young, SP; Bali, D; Kishnani, PS

Published Date

February 2014

Published In

Molecular Genetics and Metabolism

Volume / Issue

111 / 2

Start / End Page

S62 - S62

Published By

Elsevier BV

International Standard Serial Number (ISSN)

1096-7192

Digital Object Identifier (DOI)

10.1016/j.ymgme.2013.12.137