Hematopoietic stem cell gene therapy with lentiviral vector in 4 patients with cerebral X-linked adrenoleukodystrophy: long-term outcome and comparison of efficacy with allogeneic hematopoietic stem cell transplantation

Conference Paper

Full Text

Duke Authors

Cited Authors

  • Orchard, P; Cartier, N; Hacein-Bey-Abina, S; Kurtzberg, J; Escolar, M; Tolar, J; Baruchel, A; Dalle, J-H; Michel, G; Blanche, S; Bartholomae, C; Schmidt, M; Bougneres, P; Von Kalle, C; Cavazzana-Calvo, M; Fischer, A; Aubourg, P

Published Date

  • December 1, 2013

Published In

Volume / Issue

  • 24 / 12

Start / End Page

  • A21 - A21

Published By


  • 1

Electronic International Standard Serial Number (EISSN)

  • 1557-7422

International Standard Serial Number (ISSN)

  • 1043-0342

Conference Name

  • Collaborative Congress of the European-Society-for-Gene-and-Cell-Therapy and the Spanish-Society-for-Gene-and-Cell-Therapy

Conference Location

  • Madrid, SPAIN

Conference Start Date

  • October 25, 2013

Conference End Date

  • October 28, 2013