Hematopoietic Stem Cell Gene Therapy with Lentiviral Vector in 4 Patients with Cerebral X-Linked Adrenoleukodystrophy: Long-Term Outcome and Comparison of Efficacy with Allogeneic Hematopoietic Stem Cell Transplantation


Conference Paper

Full Text

Duke Authors

Cited Authors

  • Orchard, P; Cartier, N; Hacein-Bey-Abina, S; Kurtzberg, J; Escolar, M; Tolar, J; Baruchel, A; Dalle, J-H; Michel, G; Blanche, S; Bartholomae, C; Schmidt, M; Bougneres, P; van Kalle, C; Cavazzana-Calvo, M; Fischer, A; Aubourg, P

Published Date

  • June 1, 2013

Published In

Volume / Issue

  • 21 /

Start / End Page

  • S25 - S26

Published By


  • 2

Electronic International Standard Serial Number (EISSN)

  • 1525-0024

International Standard Serial Number (ISSN)

  • 1525-0016

Conference Name

  • 16th Annual Meeting of the American-Society-of-Gene-and-Cell-Therapy (ASGCT)

Conference Location

  • Salt Lake City, UT

Conference Start Date

  • May 15, 2013

Conference End Date

  • May 18, 2013