Clinical characteristics and genotypes in the ADVANCE baseline dataset, a comprehensive cohort of us children and youth with Pompe disease


Conference Paper

Full Text

Duke Authors

Cited Authors

  • Kishnani, PS; Day, JW; Gambello, M; Gibson, JB; Hillman, R; Kronn, D; Leslie, N; Pena, L; Stockton, DW; Tanpaiboon, P; Wang, R; Haack, KA; Sparks, S; Zhao, Y; Hahn, S

Published Date

  • February 2016

Published In

Volume / Issue

  • 117 / 2

Start / End Page

  • S68 - S68

Published By

International Standard Serial Number (ISSN)

  • 1096-7192

Digital Object Identifier (DOI)

  • 10.1016/j.ymgme.2015.12.323