52-week efficacy and safety profile of alglucosidase alfa produced at 4000 liter scale in US patients with Pompe disease: ADVANCE, a phase 4 open-label prospective study

Published

Conference Paper

Full Text

Published version (via Digital Object Identifier)

Duke Authors

Kishnani, Priya Sunil

Cited Authors

Hahn, S; Pena, L; Day, JW; Gambello, M; Gibson, JB; Hillman, R; Kronn, D; Stockton, D; Leslie, N; Tanpaiboon, P; Wang, R; Haack, KA; Sparks, S; Zhao, Y; Kishnani, PS

Published Date

February 2016

Published In

Molecular Genetics and Metabolism

Volume / Issue

117 / 2

Start / End Page

S54 - S54

Published By

Elsevier BV

International Standard Serial Number (ISSN)

1096-7192

Digital Object Identifier (DOI)

10.1016/j.ymgme.2015.12.281