New perspectives for ERT in Pompe disease: Extending the action of the enzyme to cytosolic targets


Conference Paper

Full Text

Duke Authors

Cited Authors

  • Sun, B; Sun, T; Armstrong, D; Yi, H; Yang, C; Austin, S; Kishnani, PS

Published Date

  • February 2016

Published In

Volume / Issue

  • 117 / 2

Start / End Page

  • S110 - S111

Published By

International Standard Serial Number (ISSN)

  • 1096-7192

Digital Object Identifier (DOI)

  • 10.1016/j.ymgme.2015.12.453