49. Minimum Effective Dose of Liver-Targeted Gene Therapy for Pompe Disease Reduced 10-Fold from Prior Estimates

Published

Conference Paper

Full Text

Duke Authors

Cited Authors

  • Han, S-O; Amson, B; Busch, K; Ronzitti, G; Li, S; Mingozzi, F; Koeberl, DD

Published Date

  • May 2016

Published In

Volume / Issue

  • 24 /

Start / End Page

  • S22 - S22

Published By

International Standard Serial Number (ISSN)

  • 1525-0016

Digital Object Identifier (DOI)

  • 10.1016/s1525-0016(16)32858-1