Survival and Developmental Milestones Among Pompe Registry Patients with Classic Infantile-Onset Pompe Disease with Different Timing of Initiation of Treatment with Enzyme Replacement Therapy.

Journal Article (Journal Article)

Full Text

Duke Authors

Cited Authors

  • Chien, Y-H; van der Ploeg, A; Jones, S; Byrne, B; Vellodi, A; Leslie, N; Mengel, E; Shankar, SP; Tanpaiboon, P; Stockton, DW; Hennermann, JB; Devecseri, Z; Kempf, J; Keutzer, J; Kishnani, P

Published Date

  • 2015

Published In

Volume / Issue

  • 2 / s1

Start / End Page

  • S61 - S62

PubMed ID

  • 27858651

International Standard Serial Number (ISSN)

  • 2214-3599


  • eng

Conference Location

  • Netherlands