Early initiation of prophylactic immune tolerance induction and enzyme replacement therapy in prenatally diagnosed infantile onset Pompe disease with a CRIM-negative mutation


Conference Paper

Full Text

Duke Authors

Cited Authors

  • Gupta, P; Shayota, B; Gomez, A; Tambini-King, L; Kazi, Z; Kishnani, PS

Published Date

  • January 2017

Published In

Volume / Issue

  • 120 / 1-2

Start / End Page

  • S60 - S60

Published By

International Standard Serial Number (ISSN)

  • 1096-7192

Digital Object Identifier (DOI)

  • 10.1016/j.ymgme.2016.11.134