Transformation in pre-treatment presentations of Gaucher disease during the first two decades of imiglucerase enzyme replacement therapy: a report from the International Collaborative Gaucher Group Gaucher Registry


Conference Paper

Full Text

Duke Authors

Cited Authors

  • Weinreb, NJ; Batista, J; Andersson, HC; Balwani, M; Andrew Burrow, T; Charrow, J; Kaplan, P; Khan, A; Kishnani, PS; Kolodny, EH; Rosenbloom, BE; Ronald Scott, C; Mistry, PK

Published Date

  • January 2017

Published In

Volume / Issue

  • 120 / 1-2

Start / End Page

  • S139 - S139

Published By

International Standard Serial Number (ISSN)

  • 1096-7192

Digital Object Identifier (DOI)

  • 10.1016/j.ymgme.2016.11.368