Correction of biochemical abnormalities and gene expression associated with improved muscle function in a phase I/II clinical trial of clenbuterol in Pompe disease patients stably treated with ERT

Published

Conference Paper

Full Text

Published version (via Digital Object Identifier)

Duke Authors

Cited Authors

Koeberl, D; Case, L; Smith, EC; Li, Y; Walters, C; Hornik, C; Thurberg, B; Bali, D; Bursac, N; Kishnani, PS

Published Date

February 2018

Published In

Molecular Genetics and Metabolism

Volume / Issue

123 / 2

Start / End Page

S79 - S80

Published By

Elsevier BV

International Standard Serial Number (ISSN)

1096-7192

Digital Object Identifier (DOI)

10.1016/j.ymgme.2017.12.202