Correction of biochemical abnormalities and gene expression associated with improved muscle function in a phase I/II clinical trial of clenbuterol in Pompe disease patients stably treated with ERT
Published
Conference Paper
Full Text
Duke Authors
Cited Authors
- Koeberl, D; Case, L; Smith, EC; Li, Y; Walters, C; Hornik, C; Thurberg, B; Bali, D; Bursac, N; Kishnani, PS
Published Date
- February 2018
Published In
Volume / Issue
- 123 / 2
Start / End Page
- S79 - S80
Published By
International Standard Serial Number (ISSN)
- 1096-7192
Digital Object Identifier (DOI)
- 10.1016/j.ymgme.2017.12.202