A prediction model to identify infantile Pompe disease (IPD) patients at high-risk of developing significant anti-drug antibodies (ADA) utilizing acid α-glucosidase (GAA ) variants and HLA-type


Conference Paper

Full Text

Duke Authors

Cited Authors

  • Kazi, Z; Desai, A; Martin, R; Terry, F; Martin, W; De Groot, A; Kishnani, P

Published Date

  • February 2018

Published In

Volume / Issue

  • 123 / 2

Start / End Page

  • S76 - S76

Published By

International Standard Serial Number (ISSN)

  • 1096-7192

Digital Object Identifier (DOI)

  • 10.1016/j.ymgme.2017.12.191