First-in-human preliminary pharmacokinetic data on a novel recombinant acid α-glucosidase, ATB200, co-administered with the pharmacological chaperone, AT2221, in patients with late-onset Pompe disease


Conference Paper

Full Text

Duke Authors

Cited Authors

  • Johnson, FK; Bratkovic, D; Byrne, B; Clemens, PR; Goker-Alpan, O; Geberhiwot, T; Kishnani, P; Ming, X; Mozaffar, T; Roberts, M; Schoser, B; Schwenkreis, P; Sivakumar, K; van der Ploeg, A; Sitaraman, S; Barth, JA; Sathe, S

Published Date

  • February 2018

Published In

Volume / Issue

  • 123 / 2

Start / End Page

  • S71 - S72

Published By

International Standard Serial Number (ISSN)

  • 1096-7192

Digital Object Identifier (DOI)

  • 10.1016/j.ymgme.2017.12.177