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Changing the clinical course of infantile Pompe disease with immune modulation strategies: 12 years of experience

Publication ,  Conference
Desai, AK; Kazi, ZB; Bali, DS; Rehder, CW; Richards, S; Rosenberg, AS; Kishnani, PS
Published in: Molecular Genetics and Metabolism
February 2019

Duke Scholars

Published In

Molecular Genetics and Metabolism

DOI

ISSN

1096-7192

Publication Date

February 2019

Volume

126

Issue

2

Start / End Page

S48 / S48

Publisher

Elsevier BV

Related Subject Headings

  • Genetics & Heredity
  • 3202 Clinical sciences
  • 3105 Genetics
  • 1103 Clinical Sciences
 

Citation

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MLA
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Desai, A. K., Kazi, Z. B., Bali, D. S., Rehder, C. W., Richards, S., Rosenberg, A. S., & Kishnani, P. S. (2019). Changing the clinical course of infantile Pompe disease with immune modulation strategies: 12 years of experience. In Molecular Genetics and Metabolism (Vol. 126, pp. S48–S48). Elsevier BV. https://doi.org/10.1016/j.ymgme.2018.12.106
Desai, Ankit K., Zoheb B. Kazi, Deeksha S. Bali, Catherine W. Rehder, Susan Richards, Amy S. Rosenberg, and Priya S. Kishnani. “Changing the clinical course of infantile Pompe disease with immune modulation strategies: 12 years of experience.” In Molecular Genetics and Metabolism, 126:S48–S48. Elsevier BV, 2019. https://doi.org/10.1016/j.ymgme.2018.12.106.
Desai AK, Kazi ZB, Bali DS, Rehder CW, Richards S, Rosenberg AS, et al. Changing the clinical course of infantile Pompe disease with immune modulation strategies: 12 years of experience. In: Molecular Genetics and Metabolism. Elsevier BV; 2019. p. S48–S48.
Desai, Ankit K., et al. “Changing the clinical course of infantile Pompe disease with immune modulation strategies: 12 years of experience.” Molecular Genetics and Metabolism, vol. 126, no. 2, Elsevier BV, 2019, pp. S48–S48. Crossref, doi:10.1016/j.ymgme.2018.12.106.
Desai AK, Kazi ZB, Bali DS, Rehder CW, Richards S, Rosenberg AS, Kishnani PS. Changing the clinical course of infantile Pompe disease with immune modulation strategies: 12 years of experience. Molecular Genetics and Metabolism. Elsevier BV; 2019. p. S48–S48.
Journal cover image

Published In

Molecular Genetics and Metabolism

DOI

ISSN

1096-7192

Publication Date

February 2019

Volume

126

Issue

2

Start / End Page

S48 / S48

Publisher

Elsevier BV

Related Subject Headings

  • Genetics & Heredity
  • 3202 Clinical sciences
  • 3105 Genetics
  • 1103 Clinical Sciences