AVXS-101 Gene-Replacement Therapy (GRT) for Spinal Muscular Atrophy Type 1 (SMA1): Pivotal Phase 3 Study (STR1VE) Update


Conference Paper

Full Text

Duke Authors

Cited Authors

  • Day, JW; Chiriboga, CA; Crawford, TO; Darras, BT; Finkel, RS; Connolly, AM; Iannaccone, ST; Kuntz, NL; Pena, LDM; Schultz, M; Shieh, PB; Smith, EC; Feltner, DE; Ogrinc, FG; Macek, TA; Wells, C; Muehring, LM; L'Italien, J; Sproule, DM; Kaspar, BK; Mendell, JR

Published Date

  • April 9, 2019

Published In

Volume / Issue

  • 92 / 15

Published By


  • 5

Electronic International Standard Serial Number (EISSN)

  • 1526-632X

International Standard Serial Number (ISSN)

  • 0028-3878

Conference Name

  • 71st Annual Meeting of the American-Academy-of-Neurology (AAN)

Conference Location

  • Philadelphia, PA

Conference Start Date

  • May 4, 2019

Conference End Date

  • May 10, 2019