Zero incidence of adeno-associated virus serotype 9 (AAV9) antibodies in a cohort of spinal muscular atrophy (SMA) type 1 patients screened in STR1VE, a pivotal phase 3 study of AVXS-101


Conference Paper

Full Text

Duke Authors

Cited Authors

  • Day, JW; Chiriboga-Klein, CA; Crawford, T; Darras, BT; Finkel, RS; Connolly, AM; Iannaccone, ST; Kuntz, NL; Pena, LDM; Schultz, M; Shieh, PB; Smith, EC; Ogrinc, F; Wells, C; Feltner, D; Sproule, D; Mendell, JR

Published Date

  • December 1, 2018

Published In

Volume / Issue

  • 29 / 12

Start / End Page

  • A82 - A83

Published By


  • 2

Electronic International Standard Serial Number (EISSN)

  • 1557-7422

International Standard Serial Number (ISSN)

  • 1043-0342

Conference Name

  • Conference on Changing the Face of Modern Medicine - Stem Cell and Gene Therapy

Conference Location

  • Lausanne, SWITZERLAND

Conference Start Date

  • October 16, 2018

Conference End Date

  • October 19, 2018