Higher dosing of alglucosidase alfa improves outcomes in children with Pompe disease

Conference Paper

Full Text

Duke Authors

Cited Authors

Khan, AA; Case, LE; Herbert, M; DeArmey, S; Jones, H; Crisp, K; Zimmerman, K; ElMallah, MK; Kishnani, PS

Published Date

February 2020

Published In

Molecular Genetics and Metabolism

Volume / Issue

129 / 2

Start / End Page

S88 - S88

Published By

Elsevier BV

International Standard Serial Number (ISSN)

1096-7192

Digital Object Identifier (DOI)

10.1016/j.ymgme.2019.11.219