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Phase 1 Study of Gene Therapy in Late-Onset Pompe Disease: Analyses of Safety and Secondary Endpoints

Publication ,  Conference
Koeberl, D; Smith, EC; Case, L; Hopkins, S; Childers, MK; Dearmey, S; Walters, C; Han, S-O; Spears, TG; Hornik, CP; Bali, D; Kishnani, PS
Published in: MOLECULAR THERAPY
2020

Duke Scholars

Published In

MOLECULAR THERAPY

EISSN

1525-0024

ISSN

1525-0016

Publication Date

2020

Volume

28

Issue

4

Start / End Page

224 / 224

Related Subject Headings

  • Biotechnology
  • 3206 Medical biotechnology
  • 3202 Clinical sciences
  • 3105 Genetics
  • 11 Medical and Health Sciences
  • 10 Technology
  • 06 Biological Sciences
 

Citation

APA
Chicago
ICMJE
MLA
NLM
Koeberl, D., Smith, E. C., Case, L., Hopkins, S., Childers, M. K., Dearmey, S., … Kishnani, P. S. (2020). Phase 1 Study of Gene Therapy in Late-Onset Pompe Disease: Analyses of Safety and Secondary Endpoints. In MOLECULAR THERAPY (Vol. 28, pp. 224–224).
Koeberl, Dwight, Edward C. Smith, Laura Case, Sam Hopkins, Martin K. Childers, Stephanie Dearmey, Crista Walters, et al. “Phase 1 Study of Gene Therapy in Late-Onset Pompe Disease: Analyses of Safety and Secondary Endpoints.” In MOLECULAR THERAPY, 28:224–224, 2020.
Koeberl D, Smith EC, Case L, Hopkins S, Childers MK, Dearmey S, et al. Phase 1 Study of Gene Therapy in Late-Onset Pompe Disease: Analyses of Safety and Secondary Endpoints. In: MOLECULAR THERAPY. 2020. p. 224–224.
Koeberl, Dwight, et al. “Phase 1 Study of Gene Therapy in Late-Onset Pompe Disease: Analyses of Safety and Secondary Endpoints.” MOLECULAR THERAPY, vol. 28, no. 4, 2020, pp. 224–224.
Koeberl D, Smith EC, Case L, Hopkins S, Childers MK, Dearmey S, Walters C, Han S-O, Spears TG, Hornik CP, Bali D, Kishnani PS. Phase 1 Study of Gene Therapy in Late-Onset Pompe Disease: Analyses of Safety and Secondary Endpoints. MOLECULAR THERAPY. 2020. p. 224–224.

Published In

MOLECULAR THERAPY

EISSN

1525-0024

ISSN

1525-0016

Publication Date

2020

Volume

28

Issue

4

Start / End Page

224 / 224

Related Subject Headings

  • Biotechnology
  • 3206 Medical biotechnology
  • 3202 Clinical sciences
  • 3105 Genetics
  • 11 Medical and Health Sciences
  • 10 Technology
  • 06 Biological Sciences