In utero enzyme replacement therapy in fetuses with lysosomal diseases: A phase I clinical trial
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Schwab, ME; Cohen, JL; Lianoglou, B; Gallagher, RC; Gonzalez-Velez, JM; Sparks, TN; Norton, ME; Gelb, MH; Wood, T; Kishnani, PS; Harmatz, PR ...
Published in: Molecular Genetics and Metabolism
February 2021
Duke Scholars
Published In
Molecular Genetics and Metabolism
DOI
ISSN
1096-7192
Publication Date
February 2021
Volume
132
Issue
2
Start / End Page
S96 / S96
Publisher
Elsevier BV
Related Subject Headings
- Genetics & Heredity
- 3202 Clinical sciences
- 3105 Genetics
- 1103 Clinical Sciences
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APA
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ICMJE
MLA
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Schwab, M. E., Cohen, J. L., Lianoglou, B., Gallagher, R. C., Gonzalez-Velez, J. M., Sparks, T. N., … MacKenzie, T. C. (2021). In utero enzyme replacement therapy in fetuses with lysosomal diseases: A phase I clinical trial. In Molecular Genetics and Metabolism (Vol. 132, pp. S96–S96). Elsevier BV. https://doi.org/10.1016/j.ymgme.2020.12.231
Schwab, Marisa E., Jennifer L. Cohen, Billie Lianoglou, Renata C. Gallagher, Juan M. Gonzalez-Velez, Teresa N. Sparks, Mary E. Norton, et al. “In utero enzyme replacement therapy in fetuses with lysosomal diseases: A phase I clinical trial.” In Molecular Genetics and Metabolism, 132:S96–S96. Elsevier BV, 2021. https://doi.org/10.1016/j.ymgme.2020.12.231.
Schwab ME, Cohen JL, Lianoglou B, Gallagher RC, Gonzalez-Velez JM, Sparks TN, et al. In utero enzyme replacement therapy in fetuses with lysosomal diseases: A phase I clinical trial. In: Molecular Genetics and Metabolism. Elsevier BV; 2021. p. S96–S96.
Schwab, Marisa E., et al. “In utero enzyme replacement therapy in fetuses with lysosomal diseases: A phase I clinical trial.” Molecular Genetics and Metabolism, vol. 132, no. 2, Elsevier BV, 2021, pp. S96–S96. Crossref, doi:10.1016/j.ymgme.2020.12.231.
Schwab ME, Cohen JL, Lianoglou B, Gallagher RC, Gonzalez-Velez JM, Sparks TN, Norton ME, Gelb MH, Wood T, Kishnani PS, Harmatz PR, MacKenzie TC. In utero enzyme replacement therapy in fetuses with lysosomal diseases: A phase I clinical trial. Molecular Genetics and Metabolism. Elsevier BV; 2021. p. S96–S96.
Published In
Molecular Genetics and Metabolism
DOI
ISSN
1096-7192
Publication Date
February 2021
Volume
132
Issue
2
Start / End Page
S96 / S96
Publisher
Elsevier BV
Related Subject Headings
- Genetics & Heredity
- 3202 Clinical sciences
- 3105 Genetics
- 1103 Clinical Sciences