339. Sustained, High-Level Expression of Human Acid Alpha-Glucosidase and Correction of Glycogen Storage Disease Type II (GSD II) with an Adeno-Associated Virus 8 (AAV2/8) Vector Containing a Liver-Specific Promoter


Conference Paper

Full Text

Duke Authors

Cited Authors

  • Franco, LM; Sun, B; Bird, A; Zhang, H; Amalfitano, A; Chen, Y-T; Koeberl, DD

Published Date

  • May 2004

Published In

Volume / Issue

  • 9 /

Start / End Page

  • S129 - S129

Published By

International Standard Serial Number (ISSN)

  • 1525-0016

Digital Object Identifier (DOI)

  • 10.1038/mt.2004.1400