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  • Breaching the Basement Membrane David R. Sherwood.  Developmental Cell.  49:498-498. 2019
  • Analysis of Postphotoactivation Scanning Diffusion Profiles for Multiple Species with Distributed Diffusion Coefficients.  Biophysical Journal.  98:400A-400A. 2010
  • Autoimmunity to Munc-18 in Rasmussen's encephalitis (vol 28, pg 375, 2000).  Neuron.  29:U22-U22. 2001
  • A model for hepatic gene therapy in cyclic neutropenia with adenoassociated virus (AAV) vectors..  American Journal of Human Genetics.  61:A356-A356. 1997
  • Investigations of candidate genes for neural tube defects implicated from mouse models..  American Journal of Human Genetics.  61:A286-A286. 1997
  • Linkage of salt sensitivity and obesity phenotypes in African Americans to marker loci on chromosome 5..  American Journal of Human Genetics.  61:A280-A280. 1997
  • Dual coupling of beta(2)-adrenergic receptor to G(i) as well as to G(s) in cardiac myocytes.  Biophysical Journal.  72:TUAM2-TUAM2. 1997
  • Expression and properties of QPs3 of mitochondrial succinate-Q reductase..  Biophysical Journal.  72:WP403-WP403. 1997
  • Telokin relaxes smooth muscle and is phosphorylated, in situ.  Biophysical Journal.  72:TU228-TU228. 1997
  • A structural basis for a phosphoramide mustard-induced DNA interstrand cross-link at 5'd(GAC).  Biophysical Journal.  70:MP447-MP447. 1996
  • Regulation of smooth muscle myosin light chain phosphatase (SMPP1M) by its 110 kDa (M110) subunit..  Biophysical Journal.  70:WPO26-WPO26. 1996
  • THE CARDIAC NA+-CA-2+ EXCHANGER BINDS TO THE CYTOSKELETAL PROTEIN ANKYRIN.  Biophysical Journal.  64:A400-A400. 1993
  • Free Energy Landscape of Casein Kinase Delta and its Implications for Circadian Rhythm.  Biophysical Journal. 207A-208A. 2020
  • Molecular Mechanism of Biased Signaling in a Prototypical G-proteincoupled Receptor.  Biophysical Journal. 162A-162A. 2020
  • A CRISPR Screen Identifies Apical Polarity Determinant Crumbs 3 as an AAV Host Restriction Factor.  Molecular Therapy. 424-425. 2019
  • AAV Gene Therapy in a Canine Model of MPS1 Prevents and Reverses Corneal Blindness.  Molecular Therapy. 441-442. 2019
  • AAV-Mediated Deletion of a Large Mutational Hotspot for Treatment of Duchenne Muscular Dystrophy.  Molecular Therapy. 377-377. 2019
  • Correction of Glycogen Storage Disease Type III with an AAV Vector Encoding a Bacterial Glycogen Debranching Enzyme.  Molecular Therapy. 17-17. 2019
  • Design Principles for AAV Mediated Circular RNA Expression in the Brain.  Molecular Therapy. 60-60. 2019
  • Engineering A Humanized AAV8 Capsid through Iterative Structure-Guided Evolution.  Molecular Therapy. 53-53. 2019
  • Exploring Novel Aptamer-Heparin Combinations to Improve Anticoagulation Therapy in Cardiopulmonary Bypass.  Molecular Therapy. 364-365. 2019
  • Inhalation of an RNA Aptamer Targeting Extracellular Histones Protects from Acute Lung Injury.  Molecular Therapy. 334-334. 2019
  • Integrase-Deficient Lentiviral Vector for Efficient CRISPR/Cas9-Mediated Gene and Epigenome-Editing Applications.  Molecular Therapy. 101-101. 2019
  • Long-Term Evaluation of AAV-CRISPR Genome Editing for Duchenne Muscular Dystrophy.  Molecular Therapy. 46-47. 2019
  • Mass Spectrometric Identification of Host Factors that Restrict AAV Vector Genome Transcription.  Molecular Therapy. 425-425. 2019
  • Physical Positioning Dramatically Improves Brain Transduction after Intrathecal Infusion of AAV9.  Molecular Therapy. 97-98. 2019
  • Reporting Long Term Survival Following Precision Tumor-Targeted Gene Delivery to Advanced Chemotherapy-Resistant Malignancies: An Academic Milestone.  Molecular Therapy. 133-133. 2019
  • Respiratory Directed Gene Therapy to Silence SOD1 Prolongs Survival in the SOD1 ALS Mouse.  Molecular Therapy. 422-422. 2019
  • Salmeterol with Liver Depot Gene Therapy Reversed Biochemical and Autophagic Abnormalities of Skeletal Muscle in Pompe Disease.  Molecular Therapy. 16-16. 2019
  • The New Epigenome-Editing Approach for Targeting Dysregulated SNCA Expression: Novel Target Validation for Next-Generation Drug Discovery.  Molecular Therapy. 35-35. 2019
  • A Single Intravenous Injection of an AAV-PHP. B Vector Encoding Human Acid alpha-Glucosidase Corrects Both Muscle and Brain Defects in Murine Pompe Disease.  Molecular Therapy. 382-383. 2018
  • Bezafibrate Enhances AAV Gene Therapy in Glycogen Storage Disease Type Ia.  Molecular Therapy. 447-447. 2018
  • Capsid-Glycan Receptor Interactions Influence AAV Transport across the Blood-Brain Barrier.  Molecular Therapy. 29-29. 2018
  • Dystrophin Restoration in a Humanized Mouse Model of Duchenne Muscular Dystrophy by Gene Editing with S. Aureus Cas9.  Molecular Therapy. 118-119. 2018
  • Long-Term Evaluation of Genome Editing Outcomes for Duchenne Muscular Dystrophy.  Molecular Therapy. 431-432. 2018
  • Mapping and Engineering Functional Domains of the Assembly Activating Protein of Adeno-Associated Viruses.  Molecular Therapy. 27-28. 2018
  • RNF121 is a Key Transcriptional Regulator of AAV Genome Expression.  Molecular Therapy. 27-27. 2018
  • Systemic Expression of Translatable Circular Rnas Using Recombinant AAV Vectors.  Molecular Therapy. 273-273. 2018
  • VSMC Specific Aptamer Ligands for the Next Generation of DES to Prevent Neointimal Formation.  Molecular Therapy. 146-146. 2018
  • Wide Spread Adenoviral Vector Delivery to a Cardiac Allograft Utilizing an Ex Vivo Perfusion Storage Strategy.  Molecular Therapy. 69-69. 2018
  • Enhancing Electrotransfection Efficiency Through Improvement in Nuclear Entry of Plasmid DNA.  Biophysical Journal. 542A-542A. 2018
  • Role of Matrix Proteins in Balancing Tissue Stiffness and Inflammation in Fibrosis.  Biophysical Journal. 23A-23A. 2018
  • Discovery of a Neurotropic Footprint That Enables AAV Transport Across the Blood-Brain Barrier.  Molecular Therapy. 230-231. 2017
  • Disruption of Water Homeostasis Affects AAV Transport Across the Blood-Brain Barrier.  Molecular Therapy. 109-109. 2017
  • Dystrophin Restoration in a Humanized Mouse Model of Duchenne Muscular Dystrophy by Gene Editing with S. aureus Cas9.  Molecular Therapy. 17-17. 2017
  • Editing out Five SERPINA1 Paralogs to Create a New Mouse Model of Genetic Emphysema.  Molecular Therapy. 117-117. 2017
  • Effect of AAV Gene Therapy on Hepatic Tumor Induced by Deficiency of Glucose-6-Phosphatase.  Molecular Therapy. 16-16. 2017
  • Expanding the CNS Transduction Profile of AAV4 by Structure-Guided Evolution.  Molecular Therapy. 247-247. 2017
  • Liver-Mediated Gene Therapy with an Engineered Secretable GAA Transgene Results in Whole-Body Correction of Pompe Disease.  Molecular Therapy. 244-244. 2017
  • Long-Term Characterization of In Vivo Genome Editing in a Mouse Model of Duchenne Muscular Dystrophy.  Molecular Therapy. 100-101. 2017
  • Salmeterol, a Beta-Agonist, Enhances Therapeutic Efficacy in Pompe Gene Therapy.  Molecular Therapy. 186-187. 2017
  • Structural Mapping of AAV9 Antigenic Sites and the Engineering of Immune Escape Variants.  Molecular Therapy. 337-337. 2017
  • Structure-Guided Iterative Evolution of Antigenically Advanced AAV Variants for Therapeutic Gene Transfer.  Molecular Therapy. 232-232. 2017
  • Systemic Delivery of AAVB1-GAA Gene Therapy for Respiratory Pathology in Pompe Disease.  Molecular Therapy. 28-29. 2017
  • Treatment of Sepsis by Neutralization of Extracellular Histones with Nucleic Acid Aptamers.  Molecular Therapy. 35-35. 2017
  • Determining the Rate of Unfolding and Refolding of FNIII Domains by Labeling Buried Cysteine.  Biophysical Journal. 289A-289A. 2014
  • Hematopoietic Stem Cell Gene Therapy with Lentiviral Vector in 4 Patients with Cerebral X-Linked Adrenoleukodystrophy: Long-Term Outcome and Comparison of Efficacy with Allogeneic Hematopoietic Stem Cell Transplantation.  Molecular Therapy. S25-S26. 2013
  • Loop 8 Plays a Role in Controlling S. Cerevisiae Kinesin-5 Cin8 Motility and Function.  Biophysical Journal. 702A-702A. 2012
  • A Structural Bistability in the Microtubule Lattice Revealed by AFM Imaging of the Inside of Microtubules.  Biophysical Journal. 449-449. 2011
  • Mitotic Functions and Motile Properties of the S. cerevisiae Kinesin-5 motors.  Biophysical Journal. 530-530. 2011
  • Neck-Linker-Length Dependence of Processive Kinesin-5 Motility.  Biophysical Journal. 122-123. 2011
  • Screening Spider Toxin Libraries for TRP Channel Inhibitors.  Biophysical Journal. 108-108. 2011
  • Stiff-Filament Microrheology.  Biophysical Journal. 557A-557A. 2010
  • Deconstructing viral capsids reveals their strengths and weaknesses.  Biophysical Journal. 49A-49A. 2007
  • BRCA1 deficient cells have increased fragile site expression that is complemented by wild type BRCA1..  American Journal of Human Genetics. 181-181. 2002
  • Apolipoprotein E allele frequencies in a population-based sample of cognitively intact Caucasians and African Americans..  American Journal of Human Genetics. A293-A293. 1997
  • Cystatin B mutations in Unverricht-Lundborg Progressive Myoclonus Epilepsy (EPM1) patients: intrafamilial instability and genotype/phenotype correlations..  American Journal of Human Genetics. A327-A327. 1997
  • Description of a novel hereditary form of capillary hemangioma and genetic mapping of predisposing chromosomal loci..  American Journal of Human Genetics. A299-A299. 1997
  • Familial aggregation of focal segmental glomerulosclerosis..  American Journal of Human Genetics. A116-A116. 1997
  • Genetic heterogeneity in familial venous malformations syndrome (FVM).  American Journal of Human Genetics. A270-A270. 1997
  • Genomic organization of RET-signaling pathway genes and mutation analysis in Hirschsprung disease patients..  American Journal of Human Genetics. A303-A303. 1997
  • Identification of a new member of the myotonic dystrophy protein kinase gene family..  American Journal of Human Genetics. A381-A381. 1997
  • Multigenic inheritance of Hirschsprung disease..  American Journal of Human Genetics. A41-A41. 1997
  • Mutation and expression analysis of the endoglin gene in Hereditary Hemorrhagic Telangiectasia reveals null alleles: A new model for pathogenesis..  American Journal of Human Genetics. A348-A348. 1997
  • An external potassium binding site revealed in DRK1, a voltage-gated K channel..  Biophysical Journal. WAMH2-WAMH2. 1997
  • Complementation of voltage sensor mutations by mutations in the pore of drk1.  Biophysical Journal. WAMH1-WAMH1. 1997
  • Microrheology in actin gels: Experiment and theory..  Biophysical Journal. TU285-TU285. 1997
  • Avidin-biotin interactions at vesicle surfaces: Adsorption and binding, cross bridge formation, and lateral interactions..  Biophysical Journal. SU359-SU359. 1996
  • Bending elasticity of individual cytoskeletal polymers measured by applying calibrated forces with optical tweezers.  Biophysical Journal. TU405-TU405. 1996
  • Structural implications of novel metal binding sites introduced into a potassium channel pore..  Biophysical Journal. MP216-MP216. 1996
  • Subunit basis for ion permeation and gating suggested by subconductance levels in K channels..  Biophysical Journal. TUAM8-TUAM8. 1996
  • Water permeability and mechanical properties of polyunsaturated lipid membranes..  Biophysical Journal. SU340-SU340. 1996