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Anaplerotic Therapy Using Triheptanoin for Patients with Glycogen Storage Disease type I

Clinical Trial Grant
Duke Scholars

Administered By

Pediatrics, Medical Genetics

Awarded By

Ultragenyx Pharmaceutical

Start Date

February 28, 2020

End Date

February 28, 2022
 

Administered By

Pediatrics, Medical Genetics

Awarded By

Ultragenyx Pharmaceutical

Start Date

February 28, 2020

End Date

February 28, 2022