A Phase 3 Randomized, Double-Blind, Placebo[1]Controlled, Global Study to Evaluate the Efficacy and Safety of Intravenous AOC 1001 for the Treatment of Myotonic Dystrophy Type 1
Clinical Trial Grant
Administered By
Neurology, Neuromuscular Disease
Awarded By
Avidity Biosciences
Start Date
August 23, 2024
End Date
December 31, 2027
Administered By
Neurology, Neuromuscular Disease
Awarded By
Avidity Biosciences
Start Date
August 23, 2024
End Date
December 31, 2027