A Post-Authorization Safety Study (PASS) to Assess Long-term Safety in Patients with Pompe Disease Treated with Avalglucosidase alfa
Clinical Trial Grant
Administered By
Pediatrics, Medical Genetics
Awarded By
Sanofi US
Start Date
September 13, 2024
End Date
December 31, 2030
Administered By
Pediatrics, Medical Genetics
Awarded By
Sanofi US
Start Date
September 13, 2024
End Date
December 31, 2030