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A Global Phase 3 Open-Label Extension Study to Assess the Long-Term Safety, Tolerability, and Efficacy of Intravenous AOC 1001 for the Treatment of Myotonic Dystrophy Type 1

Clinical Trial Grant
Duke Scholars

Administered By

Neurology, Neuromuscular Disease

Awarded By

Avidity Biosciences

Start Date

July 24, 2025

End Date

December 31, 2028
 

Administered By

Neurology, Neuromuscular Disease

Awarded By

Avidity Biosciences

Start Date

July 24, 2025

End Date

December 31, 2028