A Global Phase 3 Open-Label Extension Study to Assess the Long-Term Safety, Tolerability, and Efficacy of Intravenous AOC 1001 for the Treatment of Myotonic Dystrophy Type 1
Clinical Trial Grant
Administered By
Neurology, Neuromuscular Disease
Awarded By
Avidity Biosciences
Start Date
July 24, 2025
End Date
December 31, 2028
Administered By
Neurology, Neuromuscular Disease
Awarded By
Avidity Biosciences
Start Date
July 24, 2025
End Date
December 31, 2028