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A Phase 3 Safety and Efficacy Trial of FLT201 Gene Therapy in Patients with Gaucher Disease Type 1

Clinical Trial Grant
Duke Scholars

Administered By

Pediatrics, Medical Genetics

Awarded By

Spur Therapeutics Limited

Start Date

February 10, 2026

End Date

August 1, 2034
 

Administered By

Pediatrics, Medical Genetics

Awarded By

Spur Therapeutics Limited

Start Date

February 10, 2026

End Date

August 1, 2034