Liver-specific knockdown of M6PR with RNAi therapeutics to increase enzyme delivery to muscle tissues of Pompe disease mice during ERT
Research Grant
Administered By
Pediatrics, Medical Genetics
Awarded By
Alnylam Pharmaceuticals
Start Date
February 9, 2018
End Date
June 30, 2018
Administered By
Pediatrics, Medical Genetics
Awarded By
Alnylam Pharmaceuticals
Start Date
February 9, 2018
End Date
June 30, 2018