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Liver-specific knockdown of M6PR with RNAi therapeutics to increase enzyme delivery to muscle tissues of Pompe disease mice during ERT

Research Grant
Duke Scholars

Administered By

Pediatrics, Medical Genetics

Awarded By

Alnylam Pharmaceuticals

Start Date

February 9, 2018

End Date

June 30, 2018
 

Administered By

Pediatrics, Medical Genetics

Awarded By

Alnylam Pharmaceuticals

Start Date

February 9, 2018

End Date

June 30, 2018