Skip to main content

An open-label ascending dose cohort study to assess the safety, pharmacokinetics, and preliminary efficacy of neoGAA (GZ402666) in patients with infantile-onset Pompe disease treated with alglucosidase alfa who demonstrate clinical decline

Clinical Trial Grant
Duke Scholars

Administered By

Pediatrics, Medical Genetics

Awarded By

Sanofi US

Start Date

May 14, 2018

End Date

December 31, 2022
 

Administered By

Pediatrics, Medical Genetics

Awarded By

Sanofi US

Start Date

May 14, 2018

End Date

December 31, 2022