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A Retrospective Characterization of Response to Enzyme Replacement Therapy in Late-onset Pompe Disease

Clinical Trial Grant
Duke Scholars

Administered By

Pediatrics, Medical Genetics

Awarded By

Amicus Therapeutics Corporation

Start Date

September 15, 2017

End Date

October 19, 2018
 

Administered By

Pediatrics, Medical Genetics

Awarded By

Amicus Therapeutics Corporation

Start Date

September 15, 2017

End Date

October 19, 2018