A Retrospective Characterization of Response to Enzyme Replacement Therapy in Late-onset Pompe Disease
Clinical Trial Grant
Administered By
Pediatrics, Medical Genetics
Awarded By
Amicus Therapeutics Corporation
Start Date
September 15, 2017
End Date
October 19, 2018
Administered By
Pediatrics, Medical Genetics
Awarded By
Amicus Therapeutics Corporation
Start Date
September 15, 2017
End Date
October 19, 2018