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A Global, Phase 1/2, Open Label, Dose Escalation Study to Evaluate the Safety, Pharmacodynamics, and Pharmacokinetics of mRNA-3704 in Patients with Isolated Methylmalonic Acidemia Due to Methylmalonyl-CoA Mutase Deficiency

Clinical Trial Grant
Duke Scholars

Administered By

Pediatrics, Medical Genetics

Awarded By

Moderna Therapeutics, Inc.

Start Date

September 26, 2019

End Date

May 6, 2021
 

Administered By

Pediatrics, Medical Genetics

Awarded By

Moderna Therapeutics, Inc.

Start Date

September 26, 2019

End Date

May 6, 2021