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Enzyme replacement therapy rate escalation in infantile onset Pompe disease

Publication ,  Conference
Walters, CK; Kishnani, PS
Published in: Molecular Genetics and Metabolism
February 2016

Duke Scholars

Published In

Molecular Genetics and Metabolism

DOI

ISSN

1096-7192

Publication Date

February 2016

Volume

117

Issue

2

Start / End Page

S119 / S119

Publisher

Elsevier BV

Related Subject Headings

  • Genetics & Heredity
  • 1103 Clinical Sciences
 

Citation

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Walters, C. K., & Kishnani, P. S. (2016). Enzyme replacement therapy rate escalation in infantile onset Pompe disease. In Molecular Genetics and Metabolism (Vol. 117, pp. S119–S119). Elsevier BV. https://doi.org/10.1016/j.ymgme.2015.12.482
Walters, Crista K., and Priya S. Kishnani. “Enzyme replacement therapy rate escalation in infantile onset Pompe disease.” In Molecular Genetics and Metabolism, 117:S119–S119. Elsevier BV, 2016. https://doi.org/10.1016/j.ymgme.2015.12.482.
Walters CK, Kishnani PS. Enzyme replacement therapy rate escalation in infantile onset Pompe disease. In: Molecular Genetics and Metabolism. Elsevier BV; 2016. p. S119–S119.
Walters, Crista K., and Priya S. Kishnani. “Enzyme replacement therapy rate escalation in infantile onset Pompe disease.” Molecular Genetics and Metabolism, vol. 117, no. 2, Elsevier BV, 2016, pp. S119–S119. Crossref, doi:10.1016/j.ymgme.2015.12.482.
Walters CK, Kishnani PS. Enzyme replacement therapy rate escalation in infantile onset Pompe disease. Molecular Genetics and Metabolism. Elsevier BV; 2016. p. S119–S119.
Journal cover image

Published In

Molecular Genetics and Metabolism

DOI

ISSN

1096-7192

Publication Date

February 2016

Volume

117

Issue

2

Start / End Page

S119 / S119

Publisher

Elsevier BV

Related Subject Headings

  • Genetics & Heredity
  • 1103 Clinical Sciences