Safety and efficacy of advanced and targeted acid α-glucosidase (AT-GAA) (ATB200/AT2221) in ERT-switch nonambulatory patients with Pompe disease: preliminary results from the ATB200-02 trial
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Clemens, PR; Mozaffar, T; Schoser, B; Bratkovic, D; Byrne, BJ; Goker-Alpan, O; Roberts, M; Schwenkreis, P; Sivakumar, K; van der Ploeg, AT ...
Published in: Molecular Genetics and Metabolism
February 2019
Duke Scholars
Published In
Molecular Genetics and Metabolism
DOI
ISSN
1096-7192
Publication Date
February 2019
Volume
126
Issue
2
Start / End Page
S40 / S41
Publisher
Elsevier BV
Related Subject Headings
- Genetics & Heredity
- 3202 Clinical sciences
- 3105 Genetics
- 1103 Clinical Sciences
Citation
APA
Chicago
ICMJE
MLA
NLM
Clemens, P. R., Mozaffar, T., Schoser, B., Bratkovic, D., Byrne, B. J., Goker-Alpan, O., … Ming, X. (2019). Safety and efficacy of advanced and targeted acid α-glucosidase (AT-GAA) (ATB200/AT2221) in ERT-switch nonambulatory patients with Pompe disease: preliminary results from the ATB200-02 trial. In Molecular Genetics and Metabolism (Vol. 126, pp. S40–S41). Elsevier BV. https://doi.org/10.1016/j.ymgme.2018.12.084
Clemens, Paula R., Tahseen Mozaffar, Benedikt Schoser, Drago Bratkovic, Barry J. Byrne, Ozlem Goker-Alpan, Mark Roberts, et al. “Safety and efficacy of advanced and targeted acid α-glucosidase (AT-GAA) (ATB200/AT2221) in ERT-switch nonambulatory patients with Pompe disease: preliminary results from the ATB200-02 trial.” In Molecular Genetics and Metabolism, 126:S40–41. Elsevier BV, 2019. https://doi.org/10.1016/j.ymgme.2018.12.084.
Clemens PR, Mozaffar T, Schoser B, Bratkovic D, Byrne BJ, Goker-Alpan O, et al. Safety and efficacy of advanced and targeted acid α-glucosidase (AT-GAA) (ATB200/AT2221) in ERT-switch nonambulatory patients with Pompe disease: preliminary results from the ATB200-02 trial. In: Molecular Genetics and Metabolism. Elsevier BV; 2019. p. S40–1.
Clemens, Paula R., et al. “Safety and efficacy of advanced and targeted acid α-glucosidase (AT-GAA) (ATB200/AT2221) in ERT-switch nonambulatory patients with Pompe disease: preliminary results from the ATB200-02 trial.” Molecular Genetics and Metabolism, vol. 126, no. 2, Elsevier BV, 2019, pp. S40–41. Crossref, doi:10.1016/j.ymgme.2018.12.084.
Clemens PR, Mozaffar T, Schoser B, Bratkovic D, Byrne BJ, Goker-Alpan O, Roberts M, Schwenkreis P, Sivakumar K, van der Ploeg AT, Wright J, Sitaraman S, Barth JA, Lagast H, Kishnani P, Ming X. Safety and efficacy of advanced and targeted acid α-glucosidase (AT-GAA) (ATB200/AT2221) in ERT-switch nonambulatory patients with Pompe disease: preliminary results from the ATB200-02 trial. Molecular Genetics and Metabolism. Elsevier BV; 2019. p. S40–S41.
Published In
Molecular Genetics and Metabolism
DOI
ISSN
1096-7192
Publication Date
February 2019
Volume
126
Issue
2
Start / End Page
S40 / S41
Publisher
Elsevier BV
Related Subject Headings
- Genetics & Heredity
- 3202 Clinical sciences
- 3105 Genetics
- 1103 Clinical Sciences