First-in-human study of advanced and targeted acid α-glucosidase (AT-GAA) (ATB200/AT2221) in patients with Pompe disease: preliminary functional assessment results from the ATB200-02 trial
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Kishnani, P; Schoser, B; Bratkovic, D; Byrne, BJ; Clemens, PR; Goker-Alpan, O; Ming, X; Roberts, M; Schwenkreis, P; Sivakumar, K; Jain, V ...
Published in: Molecular Genetics and Metabolism
February 2019
Duke Scholars
Published In
Molecular Genetics and Metabolism
DOI
ISSN
1096-7192
Publication Date
February 2019
Volume
126
Issue
2
Start / End Page
S86 / S86
Publisher
Elsevier BV
Related Subject Headings
- Genetics & Heredity
- 3202 Clinical sciences
- 3105 Genetics
- 1103 Clinical Sciences
Citation
APA
Chicago
ICMJE
MLA
NLM
Kishnani, P., Schoser, B., Bratkovic, D., Byrne, B. J., Clemens, P. R., Goker-Alpan, O., … Mozaffar, T. (2019). First-in-human study of advanced and targeted acid α-glucosidase (AT-GAA) (ATB200/AT2221) in patients with Pompe disease: preliminary functional assessment results from the ATB200-02 trial. In Molecular Genetics and Metabolism (Vol. 126, pp. S86–S86). Elsevier BV. https://doi.org/10.1016/j.ymgme.2018.12.212
Kishnani, Priya, Benedikt Schoser, Drago Bratkovic, Barry J. Byrne, Paula R. Clemens, Ozlem Goker-Alpan, Xue Ming, et al. “First-in-human study of advanced and targeted acid α-glucosidase (AT-GAA) (ATB200/AT2221) in patients with Pompe disease: preliminary functional assessment results from the ATB200-02 trial.” In Molecular Genetics and Metabolism, 126:S86–S86. Elsevier BV, 2019. https://doi.org/10.1016/j.ymgme.2018.12.212.
Kishnani P, Schoser B, Bratkovic D, Byrne BJ, Clemens PR, Goker-Alpan O, et al. First-in-human study of advanced and targeted acid α-glucosidase (AT-GAA) (ATB200/AT2221) in patients with Pompe disease: preliminary functional assessment results from the ATB200-02 trial. In: Molecular Genetics and Metabolism. Elsevier BV; 2019. p. S86–S86.
Kishnani, Priya, et al. “First-in-human study of advanced and targeted acid α-glucosidase (AT-GAA) (ATB200/AT2221) in patients with Pompe disease: preliminary functional assessment results from the ATB200-02 trial.” Molecular Genetics and Metabolism, vol. 126, no. 2, Elsevier BV, 2019, pp. S86–S86. Crossref, doi:10.1016/j.ymgme.2018.12.212.
Kishnani P, Schoser B, Bratkovic D, Byrne BJ, Clemens PR, Goker-Alpan O, Ming X, Roberts M, Schwenkreis P, Sivakumar K, van der Ploeg AT, Jain V, Sitaraman S, Barth JA, Lagast H, Mozaffar T. First-in-human study of advanced and targeted acid α-glucosidase (AT-GAA) (ATB200/AT2221) in patients with Pompe disease: preliminary functional assessment results from the ATB200-02 trial. Molecular Genetics and Metabolism. Elsevier BV; 2019. p. S86–S86.
Published In
Molecular Genetics and Metabolism
DOI
ISSN
1096-7192
Publication Date
February 2019
Volume
126
Issue
2
Start / End Page
S86 / S86
Publisher
Elsevier BV
Related Subject Headings
- Genetics & Heredity
- 3202 Clinical sciences
- 3105 Genetics
- 1103 Clinical Sciences