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NEO1 and NEO-EXT studies: Long-term safety of repeat avalglucosidase alfa dosing for 4.5 years in late-onset Pompe disease patients

Publication ,  Conference
Pena, L; Barohn, RJ; Dimachkie, MM; Kishnani, PS; Ladha, S; Mengel, K-E; Sacconi, S; Van Damme, P; Vissing, J; Haack, KA; Hug, C; Johnson, J ...
Published in: Molecular Genetics and Metabolism
February 2019

Duke Scholars

Published In

Molecular Genetics and Metabolism

DOI

ISSN

1096-7192

Publication Date

February 2019

Volume

126

Issue

2

Start / End Page

S115 / S116

Publisher

Elsevier BV

Related Subject Headings

  • Genetics & Heredity
  • 3202 Clinical sciences
  • 3105 Genetics
  • 1103 Clinical Sciences
 

Citation

APA
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Pena, L., Barohn, R. J., Dimachkie, M. M., Kishnani, P. S., Ladha, S., Mengel, K.-E., … Schoser, B. (2019). NEO1 and NEO-EXT studies: Long-term safety of repeat avalglucosidase alfa dosing for 4.5 years in late-onset Pompe disease patients. In Molecular Genetics and Metabolism (Vol. 126, pp. S115–S116). Elsevier BV. https://doi.org/10.1016/j.ymgme.2018.12.294
Pena, Loren, Richard J. Barohn, Mazen M. Dimachkie, Priya S. Kishnani, Shafeeq Ladha, Karl-Eugen Mengel, Sabrina Sacconi, et al. “NEO1 and NEO-EXT studies: Long-term safety of repeat avalglucosidase alfa dosing for 4.5 years in late-onset Pompe disease patients.” In Molecular Genetics and Metabolism, 126:S115–16. Elsevier BV, 2019. https://doi.org/10.1016/j.ymgme.2018.12.294.
Pena L, Barohn RJ, Dimachkie MM, Kishnani PS, Ladha S, Mengel K-E, et al. NEO1 and NEO-EXT studies: Long-term safety of repeat avalglucosidase alfa dosing for 4.5 years in late-onset Pompe disease patients. In: Molecular Genetics and Metabolism. Elsevier BV; 2019. p. S115–6.
Pena, Loren, et al. “NEO1 and NEO-EXT studies: Long-term safety of repeat avalglucosidase alfa dosing for 4.5 years in late-onset Pompe disease patients.” Molecular Genetics and Metabolism, vol. 126, no. 2, Elsevier BV, 2019, pp. S115–16. Crossref, doi:10.1016/j.ymgme.2018.12.294.
Pena L, Barohn RJ, Dimachkie MM, Kishnani PS, Ladha S, Mengel K-E, Sacconi S, Van Damme P, Vissing J, Haack KA, Hug C, Johnson J, Sensinger C, Schoser B. NEO1 and NEO-EXT studies: Long-term safety of repeat avalglucosidase alfa dosing for 4.5 years in late-onset Pompe disease patients. Molecular Genetics and Metabolism. Elsevier BV; 2019. p. S115–S116.
Journal cover image

Published In

Molecular Genetics and Metabolism

DOI

ISSN

1096-7192

Publication Date

February 2019

Volume

126

Issue

2

Start / End Page

S115 / S116

Publisher

Elsevier BV

Related Subject Headings

  • Genetics & Heredity
  • 3202 Clinical sciences
  • 3105 Genetics
  • 1103 Clinical Sciences