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NEO1 AND NEO-EXT STUDIES: PHARMACODYNAMIC/EXPLORATORY BIOMARKER AND SAFETY ASSESSMENTS FOLLOWING REPEAT AVALGLUCOSIDASE ALFA DOSING FOR UP TO 4.5 YEARS IN PATIENTS WITH LATE-ONSET POMPE DISEASE

Publication ,  Conference
Dimachkie, M; Barohn, R; Kishnani, P; Ladha, S; Mengel, KE; Pena, LDM; Sacconi, S; Van Damme, P; Vissing, J; Haack, KA; Chen, R; Fraser, PA ...
Published in: MUSCLE & NERVE
September 1, 2019

Duke Scholars

Published In

MUSCLE & NERVE

EISSN

1097-4598

ISSN

0148-639X

Publication Date

September 1, 2019

Volume

60

Start / End Page

S48 / S49

Location

Austin, TX

Publisher

WILEY

Conference Name

Annual Meeting of the American-Association-of-Neuromuscular-and-Electrodiagnostic-Medicine (AANEM)

Related Subject Headings

  • Neurology & Neurosurgery
  • 11 Medical and Health Sciences
 

Citation

APA
Chicago
ICMJE
MLA
NLM
Dimachkie, M., Barohn, R., Kishnani, P., Ladha, S., Mengel, K. E., Pena, L. D. M., … Schoser, B. (2019). NEO1 AND NEO-EXT STUDIES: PHARMACODYNAMIC/EXPLORATORY BIOMARKER AND SAFETY ASSESSMENTS FOLLOWING REPEAT AVALGLUCOSIDASE ALFA DOSING FOR UP TO 4.5 YEARS IN PATIENTS WITH LATE-ONSET POMPE DISEASE. In MUSCLE & NERVE (Vol. 60, pp. S48–S49). Austin, TX: WILEY.
Dimachkie, Mazen, Richard Barohn, Priya Kishnani, Shafeeq Ladha, Karl Eugen Mengel, Loren D. M. Pena, Sabrina Sacconi, et al. “NEO1 AND NEO-EXT STUDIES: PHARMACODYNAMIC/EXPLORATORY BIOMARKER AND SAFETY ASSESSMENTS FOLLOWING REPEAT AVALGLUCOSIDASE ALFA DOSING FOR UP TO 4.5 YEARS IN PATIENTS WITH LATE-ONSET POMPE DISEASE.” In MUSCLE & NERVE, 60:S48–49. WILEY, 2019.
Dimachkie M, Barohn R, Kishnani P, Ladha S, Mengel KE, Pena LDM, Sacconi S, Van Damme P, Vissing J, Haack KA, Chen R, Fraser PA, Hug C, Schoser B. NEO1 AND NEO-EXT STUDIES: PHARMACODYNAMIC/EXPLORATORY BIOMARKER AND SAFETY ASSESSMENTS FOLLOWING REPEAT AVALGLUCOSIDASE ALFA DOSING FOR UP TO 4.5 YEARS IN PATIENTS WITH LATE-ONSET POMPE DISEASE. MUSCLE & NERVE. WILEY; 2019. p. S48–S49.
Journal cover image

Published In

MUSCLE & NERVE

EISSN

1097-4598

ISSN

0148-639X

Publication Date

September 1, 2019

Volume

60

Start / End Page

S48 / S49

Location

Austin, TX

Publisher

WILEY

Conference Name

Annual Meeting of the American-Association-of-Neuromuscular-and-Electrodiagnostic-Medicine (AANEM)

Related Subject Headings

  • Neurology & Neurosurgery
  • 11 Medical and Health Sciences