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NEO1 and NEO-EXT Studies: Long-Term Safety and Exploratory Efficacy of Repeat Avalglucosidase Alfa Dosing for 5.5 Years in Late-Onset Pompe Disease Patients

Publication ,  Conference
Dimachkie, M; Barohn, R; Byrne, B; Goker-Alpan, O; Kishnani, P; Ladha, S; Laforet, P; Mengel, KE; Pena, L; Sacconi, S; Straub, V; Trivedi, J ...
Published in: NEUROLOGY
2020

Duke Scholars

Published In

NEUROLOGY

EISSN

1526-632X

ISSN

0028-3878

Publication Date

2020

Volume

94

Issue

15

Related Subject Headings

  • Neurology & Neurosurgery
  • 3209 Neurosciences
  • 3202 Clinical sciences
  • 1702 Cognitive Sciences
  • 1109 Neurosciences
  • 1103 Clinical Sciences
 

Citation

APA
Chicago
ICMJE
MLA
NLM
Dimachkie, M., Barohn, R., Byrne, B., Goker-Alpan, O., Kishnani, P., Ladha, S., … Schoser, B. (2020). NEO1 and NEO-EXT Studies: Long-Term Safety and Exploratory Efficacy of Repeat Avalglucosidase Alfa Dosing for 5.5 Years in Late-Onset Pompe Disease Patients. In NEUROLOGY (Vol. 94).
Dimachkie, Mazen, Richard Barohn, Barry Byrne, Ozlem Goker-Alpan, Priya Kishnani, Shafeeq Ladha, Pascal Laforet, et al. “NEO1 and NEO-EXT Studies: Long-Term Safety and Exploratory Efficacy of Repeat Avalglucosidase Alfa Dosing for 5.5 Years in Late-Onset Pompe Disease Patients.” In NEUROLOGY, Vol. 94, 2020.
Dimachkie M, Barohn R, Byrne B, Goker-Alpan O, Kishnani P, Ladha S, Laforet P, Mengel KE, Pena L, Sacconi S, Straub V, Trivedi J, Van Damme P, van der Ploeg A, Vissing J, Young P, Haack KA, Fleurinck C, Johnson J, Liu K, Schoser B. NEO1 and NEO-EXT Studies: Long-Term Safety and Exploratory Efficacy of Repeat Avalglucosidase Alfa Dosing for 5.5 Years in Late-Onset Pompe Disease Patients. NEUROLOGY. 2020.

Published In

NEUROLOGY

EISSN

1526-632X

ISSN

0028-3878

Publication Date

2020

Volume

94

Issue

15

Related Subject Headings

  • Neurology & Neurosurgery
  • 3209 Neurosciences
  • 3202 Clinical sciences
  • 1702 Cognitive Sciences
  • 1109 Neurosciences
  • 1103 Clinical Sciences